Caliciviruses cause significant human and mammalian diseases, yet there are no calicivirus-specific antivirals available. Human norovirus (NoV) creates a substantial health burden, causing an estimated 230,000 deaths annually. Following years of intensive hepatitis C virus (HCV) research there are now 11 approved HCV antivirals available and their repurposing should be considered. These include an approved first-in-class non-nucleoside inhibitor (NNI) for class IV viruses, which targets the RNA-dependent RNA polymerase (RdRp), an essential viral replication enzyme. This study investigated the broad-spectrum antiviral activity of both HCV and NoV NNIs for treating caliciviruses.
Using a quantitative fluorescence-based RdRp assay, we identified broad-spectrum anti-calicivirus activities of four compounds: NIC02, JTK-109, TMC-647055 and Beclabuvir. NIC02 (RdRp motif B binder) is in pre-clinical studies, whilst JTK-109 (thumb I binder) development was halted in 2007 following phase II trials. However JTK-109 derivatives TMC-647055 and Beclabuvir have now advanced to phase II and III trials, respectively. Representative viruses from the Norovirus, Sapovirus and Lagovirus genera were all inhibited by JTK-109 (IC50 range: 7.6 µM – 16.6 µM) and NIC02 (IC50 range: 5.0 µM – 19.9 µM). When NIC02 and JTK109 were examined together, the two molecules exhibited combinational synergy against the NoV RdRp (CI value: 0.84). Additionally NIC02 demonstrated inhibition of two other genetically diverse RdRps; bacteriophage Φ6 RdRp (IC50 12.7 µM) and HCV RdRp (IC50 5.9 µM). Interestingly, the NoV RdRp was also susceptible to inhibition by TMC-647055 (IC50 28.3 µM) and Beclabuvir (IC50 23.8 µM). In summary, this study identified broad-spectrum NNIs which have potential as scaffolds for developing antivirals to treat calicivirus infections.